05
Oligonucleotide compounds being a component in
pharmaceutical preparations for the treatment of genetic
diseases and the repair and modulation of disease causing
mutations and protein function; RNA compounds being a
component in pharmaceutical preparations for the treatment
of genetic diseases and the repair and modulation of disease
causing mutations and protein function; RNA therapeutics for
the treatment of genetic diseases and the repair and
modulation of disease causing mutations and protein
function; Nucleic acid therapeutics for the treatment of
genetic diseases and the repair and modulation of disease
causing mutations and protein function; Oligonucleotide
compounds being a component in pharmaceutical preparations
for use in RNA editing; Oligonucleotide compounds being a
component in pharmaceutical preparations for use in base
editing; Oligonucleotide compounds being a component in
pharmaceutical preparations for use as RNA therapeutic for
the treatment of genetic diseases and the repair and
modulation of disease causing mutations and protein
function; Oligonucleotide compounds that facilitate the
editing of RNA base; Pharmaceuticals, medicines, biologics,
biotherapeutics, biosimilars and therapeutics, namely,
nucleic acid therapeutics for the treatment of genetic
diseases and the repair and modulation of disease causing
mutations and protein function; pharmaceuticals, namely,
bio-pharmaceutical preparations for the treatment of rare
diseases
40
Custom manufacture of oligonucleotides or RNAs for use in
genetic research, pharmaceutical therapies, medical research
and treatment of various conditions and disorders
42
Research and development of pharmaceutical products;
research and development in the field of bioscience;
research and development of oligonucleotide compounds for
use in targeted pharmaceutical therapies for the treatment
of various conditions, diseases and disorders, including
rare diseases, genetic disorders, liver diseases, eye
diseases, and CNS disorders; research and development of
pharmaceutical preparations for the treatment of liver-based
disorders, eye disorders and CNS disorders; research and
development of oligonucleotide compounds for targeted RNA
editing; research and development of oligonucleotide drug
platforms for use in the treatment of various conditions,
diseases and disorders, including rare diseases, genetic
disorders, liver diseases, eye diseases, and CNS disorders