05
Pharmaceutical and biological preparations based on genetic
engineering and gene therapy for use in diagnosis,
prevention, and treatment of diseases in human therapeutics;
gene therapy products, namely, biological preparations based
on engineered cells for medical use in immuno oncology,
degenerative disorders, traumatic injury, enzyme replacement
therapy, and immunology; pharmaceutical and biological
preparations based on gene, genome, and cellular editing,
modulation, and modification for use in human therapeutics;
pharmaceutical preparations, namely, therapeutic
pharmaceuticals developed through genome modifications for
the prevention and treatment of genomic disorders, including
neurological disorders, Huntington's disease, amyotrophic
lateral sclerosis (ALS), front temporal dementia, pain,
Alzheimer's, Parkinson's, ataxia, autism, epilepsy, pain,
and also including cardiovascular, peripheral nervous
system, cancer, endocrine, gastrointestinal, renal, genetic
immunological, hepatic, infectious, inflammatory, metabolic,
autoimmune, musculoskeletal, neurological, ophthalmological,
respiratory, urogenital, urological, hematologic and viral
or bacterial diseases and disorders
42
Scientific and medical research in the fields of genome
editing, gene editing, genome engineering, gene modulation,
transcriptional regulation, transcriptional modulation,
genetic diseases, gene therapy and cell therapy, and genetic
engineering research and development of pharmaceuticals,
biological preparations, diagnostic and therapeutic products
and services; design and development of engineered cells for
use in scientific research and drug discovery and
development; providing medical research and scientific
research information in the fields of genome editing, gene
editing, genome engineering, gene modulation,
transcriptional regulation, transcriptional modulation,
genetic diseases, gene therapy and cell therapy, and genetic
engineering; molecular diagnostic services for medical
research purposes
44
Molecular diagnostic services for medical purposes; medical
diagnostic testing services in the field of human disease
and human medical conditions